Research Articles
Reinventing the Genetic Tool: How a Molecular Tweak Could Unlock New Cures
Discover how AmNA-modified TFOs enhance triplex-forming ability and nuclease resistance for revolutionary gene therapy applications.
Has the Time Come? Gene Therapy's New Dawn in the Fight Against Sickle Cell Disease
Exploring the breakthrough gene therapies for sickle cell disease, their mechanisms, evidence, and implementation challenges
The Delivery Dilemma: How Viral and Non-Viral Systems Are Revolutionizing Gene Therapy
Explore how viral and non-viral gene delivery systems are transforming medicine by correcting genetic errors at their source.
The Invisible Footprint: How Gene Therapy's Building Blocks Threaten Our Waterways—and What Scientists Are Doing About It
Exploring the environmental impact of plasmid DNA production for gene therapies and innovative solutions to reduce ecological harm.